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GENETHON
FR34 patents
Top patents by PatentIndex Score
US10166272B2Jan 1, 2019
Efficient systemic treatment of dystrophic muscle pathologies
GENETHON16 citations91
US10752898B2Aug 25, 2020
Effective gene therapy tools for dystrophin exon 53 skipping
GENETHON34 citations85
US11421211B2Aug 23, 2022
Acid-alpha glucosidase variants and uses thereof
GENETHON4 citations70
US11339406B2May 24, 2022
Acid-alpha glucosidase variants and uses thereof
GENETHON3 citations70
US10786546B2Sep 29, 2020
Efficient systemic treatment of dystrophic muscle pathologies
GENETHON3 citations70
US9862934B2Jan 9, 2018
Baculovirus-based production of biopharmaceuticals free of contaminating baculoviral virions
GENETHON2 citations68
US10125352B2Nov 13, 2018
Method for producing enveloped viruses
GENETHON4 citations66
US10465169B2Nov 5, 2019
Method for purifying enveloped viruses or viral vectors
GENETHON4 citations64
US10471132B2Nov 12, 2019
Treatment of hyperbilirubinemia
GENETHON3 citations61
US11819478B2Nov 21, 2023
Selective gene therapy expression system
GENETHON0 citations60
US11499154B2Nov 15, 2022
Antisense targeting dynamin 2 and use for the treatment of centronuclear myopathies and neuropathies
GENETHON0 citations60
US11371061B2Jun 28, 2022
Compositions and methods for improving viral vector efficiency
GENETHON2 citations60
US12351816B2Jul 8, 2025
CNS gene delivery using peripheral administration of AAV vectors
GENETHON0 citations59
US12305187B2May 20, 2025
Acid-alpha glucosidase variants and uses thereof
GENETHON0 citations59
US12023366B2Jul 2, 2024
Efficient systemic treatment of dystrophic muscle pathologies
GENETHON0 citations59
US11767538B2Sep 26, 2023
Widespread gene delivery to motor neurons using peripheral injection of AAV vectors
GENETHON0 citations59
US12171843B2Dec 24, 2024
Hybrid regulatory elements
GENETHON0 citations58
US11236307B2Feb 1, 2022
Baculovirus-based production of biopharmaceuticals free of contaminating baculoviral virions
GENETHON0 citations57
US12466864B2Nov 11, 2025
Production of large-sized quasidystrophins using overlapping AAV vectors
GENETHON0 citations56
US12037362B2Jul 16, 2024
Hybrid recombinant adeno-associated virus serotype between AAV9 and AAVrh74 with reduced liver tropism
GENETHON1 citations55
US11541131B2Jan 3, 2023
Treatment of glycogen storage disease III
GENETHON0 citations54
US12582723B2Mar 24, 2026
Polynucleotides encoding a human FKRP protein
GENETHON0 citations53
US11596698B2Mar 7, 2023
Synthetic polynucleotides encoding a human FKRP protein
GENETHON0 citations53
US11104897B2Aug 31, 2021
Compositions and methods for the treatment of nucleotide repeat expansion disorders
GENETHON0 citations53
US11376321B2Jul 5, 2022
Method for removing anti-AAV antibodies from a blood-derived composition
GENETHON0 citations51
US11099193B2Aug 24, 2021
Methods for diagnosing or monitoring muscular dystrophies
GENETHON0 citations50
US9981049B2May 29, 2018
Selective gene therapy expression system
GENETHON1 citations50
US9526742B2Dec 27, 2016
Use of epigenome-modifying compounds for the treatment of genetic muscular diseases linked to a protein-conformational disorder
GENETHON1 citations50
US12012613B2Jun 18, 2024
Genetically engineered hematopoietic stem cell as a platform for systemic protein expression
GENETHON0 citations48
US10428315B2Oct 1, 2019
Baculovirus-based production of biopharmaceuticals free of contaminating baculoviral virions
GENETHON0 citations47
US11993781B2May 28, 2024
Stable pseudotyped lentiviral particles and uses thereof
GENETHON0 citations43
US11427824B2Aug 30, 2022
Compositions and methods for the treatment of myotonic dystrophy
GENETHON0 citations42
US10767192B2Sep 8, 2020
Baculovirus system for the expression of a gene therapy vector
GENETHON0 citations42
US9933438B2Apr 3, 2018
Method for diagnosing muscular dystrophy
GENETHON1 citations39