US2021198331A1PendingUtilityA1

Mic-1 compounds and use thereof

65
Assignee: NOVO NORDISK ASPriority: May 24, 2016Filed: Mar 8, 2021Published: Jul 1, 2021
Est. expiryMay 24, 2036(~9.9 yrs left)· nominal 20-yr term from priority
A61K 38/19C07K 2319/31C07K 5/1008C07K 14/475C07K 2319/00C07K 14/495C07K 5/1013A61P 3/00A61K 38/00A61K 38/27A61K 38/1841C07K 7/06C07K 7/08A61P 3/04A61K 47/642
65
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Claims

Abstract

The invention relates to MIC-1 compounds. More specifically it relates to compounds comprising a MIC-1 polypeptide and an N-terminal amino acid extension, wherein said extension consists of 3 to 36 amino acid residues and where the compound has a calculated pI lower than 6.5. The compounds of the invention have MIC-1 activity. The invention also relates to pharmaceutical compositions comprising such compounds and pharmaceutically acceptable excipients, as well as the medical use of the compounds.

Claims

exact text as granted — not AI-modified
1 . A MIC-1 compound comprising a MIC-1 polypeptide and an N-terminal amino acid extension, wherein the extension consists of 3 to 36 amino acid residues, and wherein the compound has a calculated pI lower than 6.5. 
     
     
         2 . The compound according to  claim 1 , wherein the compound is a homodimer and consists of between 218-296 amino acid residues. 
     
     
         3 . The compound according to  claim 1 , wherein the extension is in the range of 3-36 amino acid residues in length. 
     
     
         4 . The compound according to  claim 1 , wherein the extension has surplus of acidic amino acid residues selected from the group consisting of Aspartic Acid and Glutamic Acid of at least 3, 4, 5 or 6, when compared to the number of basic amino acid residues selected from the group consisting of Lysine, Arginine, and Histidine. 
     
     
         5 . The compound according to  claim 1 , wherein the extension is composed of amino acid residues selected from the group consisting of A, E, G, P, S, T, Q, and D, and wherein the extension comprises at least three E and/or D amino acid residues. 
     
     
         6 . The compound according to  claim 5 , wherein the extension comprises 6 Ser, 4 Pro, 4 Gly, 4 Thr, 4 Glu, and 2 Ala. 
     
     
         7 . The compound according to  claim 1 , wherein the extension comprises one or more of the following sequences 
       
         
           
                 
                 
               
                     
                   (SEQ ID NO: 4) 
                 
                     
                   SPAGSP, 
                 
                     
                 
                     
                   (SEQ ID NO: 5) 
                 
                     
                   TSESAT, 
                 
                     
                 
                     
                   (SEQ ID NO: 6) 
                 
                     
                   TSTEPE, 
                 
                     
                 
                     
                   (SEQ ID NO: 7) 
                 
                     
                   SEPATS, 
                 
                     
                 
                     
                   (SEQ ID NO: 8) 
                 
                     
                   TSTEEG, 
                 
                     
                 
                     
                   (SEQ ID NO: 9) 
                 
                     
                   PESGPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 10) 
                 
                     
                   SGSAPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 11) 
                 
                     
                   GSETPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 12) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEG, 
                 
                     
                 
                     
                   (SEQ ID NO: 13) 
                 
                     
                   SEPATSGSETPGTSESATPESGPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 14) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 15) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEGSPAGSP, 
                 
                     
                 
                     
                   (SEQ ID NO: 16) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGSPAGSP, 
                 
                     
                 
                     
                   (SEQ ID NO: 17) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGSPAGSP, 
                 
                     
                 
                     
                   (SEQ ID NO: 18) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEGTSESAT, 
                 
                     
                 
                     
                   (SEQ ID NO: 19) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGTSESAT, 
                 
                     
                 
                     
                   (SEQ ID NO: 20) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGTSESAT, 
                 
                     
                 
                     
                   (SEQ ID NO: 21) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEGTSTEPE, 
                 
                     
                 
                     
                   (SEQ ID NO: 22) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGTSTEPE, 
                 
                     
                 
                     
                   (SEQ ID NO: 23) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGTSTEPE, 
                 
                     
                 
                     
                   (SEQ ID NO: 24) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEGSEPATS, 
                 
                     
                 
                     
                   (SEQ ID NO: 25) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGSEPATS, 
                 
                     
                 
                     
                   (SEQ ID NO: 26) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGSEPATS, 
                 
                     
                 
                     
                   (SEQ ID NO: 27) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEGTSTEEG, 
                 
                     
                 
                     
                   (SEQ ID NO: 28) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGTSTEEG, 
                 
                     
                 
                     
                   (SEQ ID NO: 29) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGTSTEEG, 
                 
                     
                 
                     
                   (SEQ ID NO: 30) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEGPESGPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 31) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGPESGPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 32) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGPESGPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 33) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEGSGSAPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 34) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGSGSAPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 35) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGSGSAPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 36) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEGGSETPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 37) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGGSETPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 38) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGGSETPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 70) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGTSTEPS, 
                 
                     
                 
                     
                   (SEQ ID NO: 71) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGTSTEPSEG, 
                 
                     
                 
                     
                   (SEQ ID NO: 39) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEGTSESATPESGPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 40) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEGSPAGSPTSTEEG, 
                 
                     
                 
                     
                   (SEQ ID NO: 41) 
                 
                     
                   SEPATSGSETPGSPAGSPTSTEEGTSTEPESGSAPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 42) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGSPAGSPTSTEEG, 
                 
                     
                 
                     
                   (SEQ ID NO: 43) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGTSESATPESGPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 44) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGTSTEPESGSAPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 45) 
                 
                     
                   SEPATSGSETPGTSESATPESGPGSEPATSGSETPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 46) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGSPAGSPTSTEEG, 
                 
                     
                 
                     
                   (SEQ ID NO: 47) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGTSESATPESGPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 48) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGTSTEPESGSAPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 49) 
                 
                     
                   SEPATSGSETPGTSTEPESGSAPGSEPATSGSETPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 50) 
                 
                     
                   SEPATSGSETPGSEPATSGSETPGSPAGSPTSTEEG, 
                 
                     
                 
                     
                   (SEQ ID NO: 51) 
                 
                     
                   SEPATSGSETPGSEPATSGSETPGTSESATPESGPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 52) 
                 
                     
                   SEPATSGSETPGSEPATSGSETPGTSTEPESGSAPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 53) 
                 
                     
                   SEPATSGSETPGSEPATSGSETPGSEPATSGSETPG, 
                 
                     
                 
                     
                   (SEQ ID NO: 136) 
                 
                     
                   GGGS, 
                 
                     
                 
                     
                   (SEQ ID NO: 137) 
                 
                     
                   GSGS, 
                 
                     
                 
                     
                   (SEQ ID NO: 138) 
                 
                     
                   GGSS 
                 
                     
                   and 
                 
                     
                 
                     
                   (SEQ ID NO: 139) 
                 
                     
                   SSSG. 
                 
             
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
               
            
           
         
       
     
     
         8 . The compound according to  claim 1 , wherein the extension comprises one or more of the following sequences 
       
         
           
                 
                 
               
                     
                   (SEQ ID NO: 118) 
                 
                     
                   GEPS, 
                 
                     
                 
                     
                   (SEQ ID NO: 119) 
                 
                     
                   GPSE, 
                 
                     
                 
                     
                   (SEQ ID NO: 120) 
                 
                     
                   GPES, 
                 
                     
                 
                     
                   (SEQ ID NO: 121) 
                 
                     
                   GSPE, 
                 
                     
                 
                     
                   (SEQ ID NO: 122) 
                 
                     
                   GSEP, 
                 
                     
                 
                     
                   (SEQ ID NO: 140) 
                 
                     
                   GEPSGEPSGEPSGEPSGEPS, 
                 
                     
                 
                     
                   (SEQ ID NO: 141) 
                 
                     
                   GPSEGPSEGPSEGPSEGPSE, 
                 
                     
                 
                     
                   (SEQ ID NO: 142) 
                 
                     
                   GPESGPESGPESGPESGPES, 
                 
                     
                 
                     
                   (SEQ ID NO: 143) 
                 
                     
                   GSPEGSPEGSPEGSPEGSPE, 
                 
                     
                 
                     
                   (SEQ ID NO: 144) 
                 
                     
                   GSEPGSEPGSEPGSEPGSE, 
                 
                     
                 
                     
                   (SEQ ID NO: 123) 
                 
                     
                   GEPQ, 
                 
                     
                 
                     
                   (SEQ ID NO: 124) 
                 
                     
                   GEQP, 
                 
                     
                 
                     
                   (SEQ ID NO: 125) 
                 
                     
                   GPEQ, 
                 
                     
                 
                     
                   (SEQ ID NO: 126) 
                 
                     
                   GPQE, 
                 
                     
                 
                     
                   (SEQ ID NO: 127) 
                 
                     
                   GQEP, 
                 
                     
                 
                     
                   (SEQ ID NO: 128) 
                 
                     
                   GQPE, 
                 
                     
                 
                     
                   (SEQ ID NO: 145) 
                 
                     
                   GEPQGEPQGEPQGEPQGEPQ, 
                 
                     
                 
                     
                   (SEQ ID NO: 146) 
                 
                     
                   GEQPGEQPGEQPGEQPGEQP, 
                 
                     
                 
                     
                   (SEQ ID NO: 147) 
                 
                     
                   GPEQGPEQGPEQGPEQGPEQ, 
                 
                     
                 
                     
                   (SEQ ID NO: 148) 
                 
                     
                   GPQEGPQEGPQEGPQEGPQE, 
                 
                     
                 
                     
                   (SEQ ID NO: 149) 
                 
                     
                   GQEPGQEPGQEPGQEPGQEP, 
                 
                     
                 
                     
                   (SEQ ID NO: 150) 
                 
                     
                   GQPEGQPEGQPEGQPEGQPE, 
                 
                     
                 
                     
                   (SEQ ID NO: 136) 
                 
                     
                   GGGS, 
                 
                     
                 
                     
                   (SEQ ID NO: 137) 
                 
                     
                   GSGS, 
                 
                     
                 
                     
                   (SEQ ID NO: 138) 
                 
                     
                   GGSS 
                 
                     
                   and 
                 
                     
                 
                     
                   (SEQ ID NO: 139) 
                 
                     
                   SSSG. 
                 
             
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
               
            
           
         
       
     
     
         9 . The compound according to  claim 1 , wherein the extension comprises one or more of the following sequences 
       
         
           
                 
                 
               
                     
                   (SEQ ID NO: 129) 
                 
                     
                   PEDEETPEQE, 
                 
                     
                 
                     
                   (SEQ ID NO: 130) 
                 
                     
                   PDEGTEEETE, 
                 
                     
                 
                     
                   (SEQ ID NO: 131) 
                 
                     
                   PAAEEEDDPD, 
                 
                     
                 
                     
                   (SEQ ID NO: 132) 
                 
                     
                   AEPDEDPQSED, 
                 
                     
                 
                     
                   (SEQ ID NO: 133) 
                 
                     
                   AEPDEDPQSE, 
                 
                     
                 
                     
                   (SEQ ID NO: 134) 
                 
                     
                   AEPEEQEED, 
                 
                     
                 
                     
                   (SEQ ID NO: 135) 
                 
                     
                   AEPEEQEE, 
                 
                     
                 
                     
                   (SEQ ID NO: 151) 
                 
                     
                   AEEAEEAEEAEEAEE, 
                 
                     
                 
                     
                   (SEQ ID NO: 136) 
                 
                     
                   GGGS, 
                 
                     
                 
                     
                   (SEQ ID NO: 137) 
                 
                     
                   GSGS, 
                 
                     
                 
                     
                   (SEQ ID NO: 138) 
                 
                     
                   GGSS 
                 
                     
                   and 
                 
                     
                 
                     
                   (SEQ ID NO: 139) 
                 
                     
                   SSSG. 
                 
             
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
               
            
           
         
       
     
     
         10 . The compound according to  claim 1 , wherein the MIC-1 polypeptide displays at least 85% sequence identity to MIC-1 of SEQ ID NO:1. 
     
     
         11 . The compound according to  claim 1  wherein the MIC-1 polypeptide comprise one or more of the following substitutions N3E, P11E, H18E, R21E, A30E, A47E, R53E, A54E, M57E, M57L, H66E, R67E, L68E, K69E, A75E, A81E, P85E, M86L, Q90E, T92E, L105E, and K107E, when compared to SEQ ID NO:1. 
     
     
         12 . The compound according to  claim 1  wherein the MIC-1 polypeptide comprise a deletion of the first three residues (MIC-1-Δ1-3) or a deletion of N3 (des-N3), when compared SEQ ID NO:1. 
     
     
         13 . A MIC-1 compound comprising a MIC-1 polypeptide and an N-terminal amino acid extension, wherein the compound comprises an amino acid sequence according to a sequence selected from the group consisting of: SEQ ID NO: 100, 104, 106, 107, 108, 109, 111, 112, 113, 114, 115, 116, 117 and 164. 
     
     
         14 . The compound according to  claim 1 , wherein the compound has a solubility of 0.5, 1.0, 5.0, 10, 30 or 50 mg/ml at pH 8.0 in a Tris buffer system. 
     
     
         15 . A method for treating a metabolic disorder, comprising administering the compound according to  claim 1  to a person in need thereof, wherein the metabolic disorder is selected from the group consisting of obesity, diabetes, cardiovascular like dyslipidaemia, arteriosclerosis, steatohepatitis, and diabetic nephropathy.

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