US2022257564A1PendingUtilityA1

Pharmaceutical compositions for treating cystic fibrosis

66
Assignee: VERTEX PHARMAPriority: Feb 5, 2018Filed: Sep 15, 2021Published: Aug 18, 2022
Est. expiryFeb 5, 2038(~11.6 yrs left)· nominal 20-yr term from priority
A61P 43/00A61K 9/2095A61K 31/47A61K 31/4045A61K 31/4439A61K 9/2027A61K 9/2054A61K 31/404A61P 11/00A61K 2300/00A61K 31/443A61P 25/28
66
PatentIndex Score
0
Cited by
0
References
0
Claims

Abstract

A pharmaceutical composition comprising Compound I: Methods of treating cystic fibrosis comprising administering one or more of such pharmaceutical compositions to a patient.

Claims

exact text as granted — not AI-modified
1 . A pharmaceutical composition comprising
 (a) 75 mg to 125 mg of Compound I:   
       
         
           
           
               
               
           
         
         (b) a first solid dispersion comprising 25 mg to 75 mg of Compound II: 
       
       
         
           
           
               
               
           
         
       
       and 10 wt % to 30 wt % of a polymer relative to the total weight of the first solid dispersion; and 
       (c) a second solid dispersion comprising 50 mg to 100 mg of Compound III: 
       
         
           
           
               
               
           
         
       
       and 10 wt % to 30 wt % of a polymer relative to the total weight of the second solid dispersion. 
     
     
         2 . The pharmaceutical composition of  claim 1 , comprising
 75 mg to 125 mg of Compound I; and wherein the first solid dispersion comprises 50 mg of Compound II; and the second solid dispersion comprises 75 mg of Compound III.   
     
     
         3 . A pharmaceutical composition comprising:
 (a) Compound I:   
       
         
           
           
               
               
           
         
       
       (b) 
       a first solid dispersion comprising 70 wt % to 90 wt % of Compound II relative to the total weight of the first solid dispersion: 
       
         
           
           
               
               
           
         
       
       and 10 wt % to 30 wt % of a polymer relative to the total weight of the first solid dispersion; and 
       (c) 
       a second solid dispersion comprising 70 wt % to 90 wt % of Compound III relative to the total weight of the second solid dispersion: 
       
         
           
           
               
               
           
         
       
       and 10 wt % to 30 wt % of a polymer relative to the total weight of the second solid dispersion, wherein the the weight ratio of Compound I in (a):Compound II in (b):Compound III in (c) is in a range of 4:2:3-6. 
     
     
         4 . (canceled) 
     
     
         5 . (canceled) 
     
     
         6 . (canceled) 
     
     
         7 . The pharmaceutical composition of  claim 1 , wherein Compound I is Crystalline Form A. 
     
     
         8 . The pharmaceutical composition of  claim 7 , wherein Compound I Crystalline Form A is in substantially pure form. 
     
     
         9 . The pharmaceutical composition of  claim 7 , wherein Compound I Crystalline Form A is characterized by an X-ray powder diffractogram having a signal at at least three two-theta values chosen from 6.6±0.2, 7.6±0.2, 9.6±0.2, 12.4±0.2, 13.1±0.2, 15.2±0.2, 16.4±0.2, 18.2±0.2, and 18.6±0.2. 
     
     
         10 . A method of treating cystic fibrosis in a patient comprising orally administering to the patient one or more of the pharmaceutical composition of  claim 1 . 
     
     
         11 . The method according to  claim 10 , wherein said patient having cystic fibrosis is chosen from patients with F508del/minimal function genotypes, patients with F508del/F508del genotypes, patients with F508del/gating genotypes, and patients with F508del/residual function genotypes. 
     
     
         12 . (canceled) 
     
     
         13 . (canceled) 
     
     
         14 . The pharmaceutical composition of  claim 3 , wherein at least one of the first and second solid dispersions is a spray-dried dispersion. 
     
     
         15 . The pharmaceutical composition of  claim 3 , wherein both of the first and second solid dispersions are spray-dried dispersions. 
     
     
         16 . The pharmaceutical composition of  claim 3 , wherein said polymer in the first solid dispersion is hydroxypropyl methylcellulose; and said polymer in the second solid dispersion is hydroxypropyl methylcellulose acetate succinate. 
     
     
         17 . The pharmaceutical composition of  claim 3 , wherein:
 the first solid dispersion comprises 70 wt % to 85 wt % of Compound II relative to the total weight of the first solid dispersion, and the polymer is hydroxypropyl methylcellulose in an amount of 15 wt % to 30 wt % relative to the total weight of the first solid dispersion; and   the second solid dispersion comprises 70 wt % to 85 wt % of Compound III relative to the total weight of the second solid dispersion, 0.5% sodium lauryl sulfate relative to the total weight of the second solid dispersion, and the polymer is hydroxypropyl methylcellulose acetate succinate in an amount of 14.5 wt % to 29.5 wt % relative to the total weight of the second solid dispersion.   
     
     
         18 . The pharmaceutical composition of  claim 3 , wherein the first solid dispersion comprises 80 wt % of Compound II relative to the total weight of the first solid dispersion; and 20 wt % of hydroxypropyl methylcellulose relative to the total weight of the first solid dispersion. 
     
     
         19 . The pharmaceutical composition of  claim 3 , wherein the second solid dispersion comprises 80 wt % of Compound III relative to the total weight of the second solid dispersion; 0.5% of sodium lauryl sulfate relative to the total weight of the second solid dispersion, and 19.5 wt % of hydroxypropyl methylcellulose acetate succinate relative to the total weight of the second solid dispersion. 
     
     
         20 . The pharmaceutical composition of  claim 3 , further comprising one or more pharmaceutically acceptable excipients chosen from one or more fillers, disintegrants, and lubricants. 
     
     
         21 . The pharmaceutical composition of  claim 3 , wherein:
 said fillers are chosen from microcrystalline cellulose, silicified microcrystalline cellulose, lactose, dicalcium phosphate, mannitol, copovidone, hydroxypropyl cellulose, hydroxypropyl methylcellulose, methyl cellulose, ethyl cellulose, starch, Maltodextrin, agar, and guar gum;   said disintegrants are chosen from croscarmellose sodium, sodium starch glycolate, crospovidone, corn or pre-gelatinized starch, sodium carboxymethyl cellulose, calcium carboxymethyl cellulose, and microcrystalline cellulose; and   said lubricants are chosen from magnesium stearate, sodium stearyl fumarate, calcium stearate, sodium stearate, stearic acid, and talc.   
     
     
         22 . The pharmaceutical composition of  claim 3 , wherein
 Compound I is substantially crystalline, and wherein each of Compounds II and III is independently substantially amorphous.   
     
     
         23 . The pharmaceutical composition of  claim 3 , wherein the pharmaceutical composition is a tablet or in the form of granules. 
     
     
         24 . The pharmaceutical composition of  claim 3 , wherein the pharmaceutical composition further comprises microcrystalline cellulose; croscarmellose sodium; and
 magnesium stearate.   
     
     
         25 . The pharmaceutical composition of  claim 3 , wherein the pharmaceutical composition comprises 15 wt % to 45 wt % of microcrystalline cellulose relative to the total weight of the pharmaceutical composition; 1 wt % to 10 wt % of croscarmellose sodium relative to the total weight of the pharmaceutical composition; and 0.5 wt % to 3 wt % mg of magnesium stearate relative to the total weight of the pharmaceutical composition. 
     
     
         26 . The pharmaceutical composition of  claim 1 , wherein the pharmaceutical composition comprises 80 mg to 120 mg of Compound I. 
     
     
         27 . The pharmaceutical composition of  claim 1 , wherein the pharmaceutical composition comprises 100 mg of Compound I; and wherein the first solid dispersion comprises 50 mg of Compound II; and the second solid dispersion comprises 75 mg of Compound III. 
     
     
         28 . A single tablet having the following formulation: 
       
         
           
                 
                 
                 
               
                     
                     
                 
                     
                     
                   mg per 
                 
                     
                   Material Name 
                   tablet 
                 
                     
                     
                 
                     
                 
                 
                 
                 
                 
               
                     
                   Intra Granular 
                   Compound I 
                   100 
                 
                     
                     
                   Compound II SDD (80 wt % 
                   62.5 
                 
                     
                     
                   Compound II and 20 wt % 
                 
                     
                     
                   HPMC) 
                 
                     
                     
                   Compound III SDD (80 wt % 
                   93.8 
                 
                     
                     
                   Compound III, 19.5 wt % 
                 
                     
                     
                   HPMCAS, and 0.5 wt % 
                 
                     
                     
                   sodium lauryl sulfate) 
                 
                     
                     
                   Croscarmellose sodium 
                   29.3 
                 
                     
                     
                   Microcrystalline cellulose 
                   80.5 
                 
                     
                   Extra Granular 
                   Microcrystalline cellulose 
                   117.1 
                 
                     
                     
                   Magnesium stearate 
                   4.9 
                 
                 
                 
                 
               
                     
                   Total Core Tablet 
                   488 
                 
                 
                 
                 
               
                     
                   Film coat 
                   14.6 
                 
                 
                 
                 
               
                     
                   Total Coated Tablet 
                   502.6. 
                 
                     
                     
                 
             
                
                
                
                
               
               
                
               
            
             
                
                
                
                
                
                
                
                
                
                
                
                
               
            
             
                
               
            
             
                
               
            
             
                
                
               
            
           
         
       
     
     
         29 . A single tablet having the following formulation: 
       
         
           
                 
                 
                 
               
                     
                     
                 
                     
                     
                   mg per 
                 
                     
                   Component 
                   tablet 
                 
                     
                     
                 
                     
                 
                 
                 
                 
                 
               
                     
                   Intragranular 
                   Compound I 
                   50.0 
                 
                     
                     
                   a solid dispersion comprising: 
                   31.3 
                 
                     
                     
                   80 wt % substantially amorphous 
                 
                     
                     
                   Compound II, and 20 wt % HPMC 
                 
                     
                     
                   a solid dispersion comprising: 
                   46.9 
                 
                     
                     
                   80 wt % substantially amorphous 
                 
                     
                     
                   Compound III, 
                 
                     
                     
                   19.5 wt % HPMCAS, and 
                 
                     
                     
                   0.5 wt % sodium lauryl sulfate 
                 
                     
                     
                   Croscarmellose sodium 
                   14.6 
                 
                     
                     
                   Microcrystaline cellulose 
                   40.2 
                 
                     
                   Extragranular 
                   Microcrystaline cellulose 
                   58.6 
                 
                     
                     
                   Magnesium stearate 
                   2.4 
                 
                 
                 
                 
               
                     
                   Total Core Tablet 
                   244.0 
                 
                 
                 
                 
               
                     
                   Film coat 
                   7.3 
                 
                 
                 
                 
               
                     
                   Total 
                   251.3.

Cited by (0)

No later patents cite this yet.

References (0)

No backward citations on record.