US2023398238A1PendingUtilityA1

Targeted contrast agents for mri of alpha-synuclein deposition

64
Assignee: Texas Childrens HospitalPriority: Feb 12, 2020Filed: Aug 24, 2023Published: Dec 14, 2023
Est. expiryFeb 12, 2040(~13.6 yrs left)· nominal 20-yr term from priority
A61K 49/085C07C 49/755C07C 65/40C07D 333/22A61K 49/1812A61K 47/542A61K 47/545A61K 9/1271A61K 49/108A61K 47/544C07F 9/106C07F 9/655345C07C 2602/08
64
PatentIndex Score
0
Cited by
0
References
0
Claims

Abstract

A liposomal composition (“ADx-003”) is provided, ADx-003 comprising a first phospholipid; a sterically bulky excipient that is capable of stabilizing the liposomal composition; a second phospholipid that is derivatized with a first polymer; a macrocyclic gadolinium-based imaging agent; and a third phospholipid that is derivatized with a second polymer, the second polymer being conjugated to a targeting ligand, the targeting ligand being represented by Formula I: wherein X is —CH 2 —, —CH 2 —CH 2 —, —CHO—, or —O—CO—; Y is —CH—CH═CH— or A and B are independently selected from C and N; R 1 , R 2 , R 3 , and R 4 are independently selected from —H, halogen, —OH, and —CH 3 ; and R 5 , R 6 , and R 7 are independently selected from —H, halogen, —OH, —OCH 3 , —NO 2 , —N(CH 3 ) 2 , C 1 -C 6 alkyl, or a substituted or unsubstituted C 4 -C 6 aryl group, except that when A and/or B is N the adjacent R 5 and/or R 7 is —H, or a pharmaceutically acceptable salt thereof.

Claims

exact text as granted — not AI-modified
What is claimed is: 
     
         1 . A compound according to Formula I: 
       
         
           
           
               
               
           
         
         wherein 
         X is —CH 2 —, —CH 2 —CH 2 —, —CHO—, or —O—CO—; 
         Y is —CH—CH═CH— or 
       
       
         
           
           
               
               
           
         
         A and B are independently selected from C and N; 
         R 1 , R 2 , R 3  and R 4  are independently selected from —H, Halogen, —OH, and -Me; and 
         R 5 , R 6 , and R 7  are independently selected from —H, Halogen, —OH, —OMe, —NO 2 , —NMe 2 , C 1 -C 6  alkyl, or a substituted or unsubstituted C 4 -C 6  aryl group, except that when A and/or B is N the adjacent R 5  and/or R 7  is —H, or a pharmaceutically acceptable salt thereof. 
       
     
     
         2 . The compound of  claim 1 , wherein the compound has the structure: 
       
         
           
           
               
               
           
         
       
     
     
         3 . The compound of  claim 1 , wherein the compound has the structure: 
       
         
           
           
               
               
           
         
       
     
     
         4 . The compound of  claim 1 , wherein the compound has the structure: 
       
         
           
           
               
               
           
         
       
     
     
         5 . A phospholipid-polymer-targeting ligand conjugate, wherein:
 the phospholipid-polymer comprises:   
       
         
           
           
               
               
           
         
         
           wherein the variable n is any integer from about 70 to about 90, and wherein the variable m is one of: 12, 13, 14, 15, 16, 17, or 18; and 
         
         the targeting ligand comprises a compound according to Formula I: 
       
       
         
           
           
               
               
           
         
         wherein
 X is —CH 2 —, —CH 2 —CH 2 —, —CHO—, or —O—CO—; 
 Y is —CH—CH═CH— or 
 
       
       
         
           
           
               
               
           
         
         
           A and B are independently selected from C and N; 
           R 1 , R 2 , R 3  and R 4  are independently selected from —H, Halogen, —OH, and -Me; and 
           R 5 , R 6 , and R 7  are independently selected from —H, Halogen, —OH, —OMe, —NO 2 , —NMe 2 , C 1 -C 6  alkyl, or a substituted or unsubstituted C 4 -C 6  aryl group, except that when A and/or B is N the adjacent R 5  and/or R 7  is —H, or a pharmaceutically acceptable salt thereof. 
         
       
     
     
         6 . The phospholipid-polymer-targeting ligand conjugate of  claim 5 , comprising: 
       
         
           
           
               
               
           
         
       
       wherein n is 77 or 79. 
     
     
         7 . The phospholipid-polymer-targeting ligand conjugate of  claim 5 , comprising: 
       
         
           
           
               
               
           
         
         wherein n is 77 or 79. 
       
     
     
         8 . The phospholipid-polymer-targeting ligand conjugate of  claim 5 , comprising: 
       
         
           
           
               
               
           
         
         wherein n is 77 or 79. 
       
     
     
         9 . A liposomal composition, comprising:
 a first phospholipid;   a sterically bulky excipient that is capable of stabilizing the liposomal composition;   a second phospholipid that is derivatized with a first polymer;   a macrocyclic gadolinium-based imaging agent; and   a third phospholipid that is derivatized with a second polymer, the second polymer being conjugated to a targeting ligand, the targeting ligand being represented by a compound according to Formula I:   
       
         
           
           
               
               
           
         
         wherein
 X is —CH 2 —, —CH 2 —CH 2 —, —CHO—, or —O—CO—; 
 Y is —CH—CH═CH— or 
 
       
       
         
           
           
               
               
           
         
         
           A and B are independently selected from C and N; 
           R 1 , R 2 , R 3  and R 4  are independently selected from —H, Halogen, —OH, and -Me; and 
         
         R 5 , R 6 , and R 7  are independently selected from —H, Halogen, —OH, —OMe, —NO 2 , —NMe 2 , C 1 -C 6  alkyl, or a substituted or unsubstituted C 4 -C 6  aryl group, except that when A and/or B is N the adjacent R 5  and/or R 7  is —H, or a pharmaceutically acceptable salt thereof. 
       
     
     
         10 . The liposomal composition of  claim 9 , wherein the first phospholipid comprises hydrogenated soy L-α-phosphatidylcholine (“HSPC”). 
     
     
         11 . The liposomal composition of  claim 9 , wherein the sterically bulky excipient that is capable of stabilizing the liposomal composition comprises cholesterol (“Chol”). 
     
     
         12 . The liposomal composition of  claim 9 , wherein the second phospholipid that is derivatized with a first polymer comprises 1,2-distearoyl-sn-glycero-3-phosphoethanolamine-N-(methoxy (polyethylene glycol)-2000) (“DSPE-mPEG2000”). 
     
     
         13 . The liposomal composition of  claim 9 , wherein the macrocyclic gadolinium-based imaging agent comprises: 
       
         
           
           
               
               
           
         
       
     
     
         14 . The liposomal composition of  claim 9 , wherein the macrocyclic gadolinium-based imaging agent is conjugated to a fourth phospholipid to comprise: 
       
         
           
           
               
               
           
         
       
       or a salt thereof, and wherein the variable x is one of: 12, 13, 14, 15, 16, 17, or 18. 
     
     
         15 . The liposomal composition of  claim 14 , wherein the variable x is 16 (the conjugate: “Gd(III)-DOTA-DSPE”). 
     
     
         16 . The liposomal composition of  claim 9 , wherein the targeting ligand comprises: 
       
         
           
           
               
               
           
         
       
     
     
         17 . The liposomal composition of  claim 9 , wherein the targeting ligand comprises: 
       
         
           
           
               
               
           
         
       
     
     
         18 . The liposomal composition of  claim 9 , wherein the targeting ligand comprises: 
       
         
           
           
               
               
           
         
       
     
     
         19 . The liposomal composition of  claim 9 , wherein the third phospholipid that is derivatized with a second polymer comprises: 
       
         
           
           
               
               
           
         
       
       or a salt thereof, wherein the variable n is any integer from about 70 to about 90, and wherein the variable m is one of: 12, 13, 14, 15, 16, 17, or 18. 
     
     
         20 . The liposomal composition of  claim 9 , wherein the conjugate of the third phospholipid, the second polymer, and the targeting ligand comprises: 
       
         
           
           
               
               
           
         
         wherein n is 77 or 79.

Cited by (0)

No later patents cite this yet.

References (0)

No backward citations on record.