USRE48335EActiveUtility

Polymyxin derivatives as antimicrobial compounds

60
Assignee: UNIV MONASHPriority: Apr 1, 2014Filed: Apr 1, 2015Granted: Dec 1, 2020
Est. expiryApr 1, 2034(~7.7 yrs left)· nominal 20-yr term from priority
Y02A50/30A61K 38/12A61P 43/00A61P 31/04C07K 7/62A61K 38/00
60
PatentIndex Score
1
Cited by
22
References
4
Claims

Abstract

The present invention relates to antimicrobial compounds and their uses, and in particular to peptide antibiotics which may be used in the treatment of bacterial infections such as Gram-negative bacterial infections, particularly those caused by multidrug-resistant (MDR) pathogens.

Claims

exact text as granted — not AI-modified
The claims defining the invention are as follows: 
     
       1. A compound of formula (IIb): 
       
         
           
           
               
               
           
         
         wherein: 
         R 1  is selected from hexanoyl, hepatanoyl, octanoyl, nonanoyl, decanoyl, dodecanoyl, 7 methyloctanoyl, S-5-methylheptanoyl, R-5-methylheptanoyl, S,R-5-methylheptanoyl (racemic mixture), 4-biphenylcarboxyl, 4-trifluoromethylbenzoyl, 4-ethylbenzoyl, 3,4-dichlorobenzoyl, 4-chlorobenzoyl, 3-chlorobenzoyl, pentafluorobenzoyl, 4-methylbenzoyl, 4-ethylphenylacetyl, phenylacetyl, 4-methylphenylacetyl, 4-trifluoromethylphenylacetyl, pentafluorophenylacetyl, 3,4-dichlorophenylacetyl, 4-chlorophenylacetyl, 3-chlorophenylacetyl, 2-chlorobenzoyl, 2-fluorobenzoyl, 2-methylbenzoyl, 2-chlorophenylacetyl, 2-fluorophenylacetyl, 2-methylphenylacetyl, 2,3-dichlorobenzoyl, 2,3-dimethylbenzoyl, 2,4-dichlorophenylacetyl, 2,4-dichlorobenzoyl, 2,4-dimethylbenzoyl, 2-chloro-4-methylbenzoyl, 2-chloro-4-trifluoromethylbenzoyl, 3-fluorobenzoyl, 3-methylbenzoyl, 3-trifuoromethylbenzoyl, 3,4-dimethylbenzoyl, 3-fluoro-4-methylbenzoyl, 4-chloro-3-methylbenzoyl, 3,4-dimethylphenylacetyl, 3-chloro-4-methylbenzoyl, 4-chloro-3-fluorobenzoyl, 3-fluoro-4-trifluoromethylbenzoyl, 3-chloro-4-fluorobenzoyl, 4-methyl-3-trifluoromethylbenzoyl, 3-methyl-4-trifluoromethylbenzoyl, 3-methyl-5-trifluoromethylbenzoyl, 3,5-dimethylbenzoyl, 3,5-dichlorobenzoyl, 3,5-bis(trifluoromethyl) benzoyl, 3-fluoro-5-trifluoromethylbenzoyl, 3-chloro-5-methylbenzoyl, 3-chloro-5-fluorobenzoyl, 2,4,6-trimethylbenzoyl, 2,4,6-trichlorobenzoyl, 2-chloro-4-fluorobenzoyl, 4-chloro-2-fluorobenzoyl, 3,4,5-trifluoromethylbenzoyl, 4-chloro-2-trifluoromethylbenzoyl, 2-fluoro-4-trifluoromethylbenzoyl, 3-biphenylcarboxyl, 4-chlorobiphenyl-4-carboxyl, 3-phenylproponyl, 4-phenylbutanoyl, 2,4-dichlorophenylsulfonyl, 4-chloro-3-trifluoromethylbenzoyl, 4-isopropylbenzoyl, 4-chloro-3-fluorobenzoyl, and 3-chloro-4-trifluoromethylbenzoyl; 
         R 3  represents a side chain of an amino acid selected from leucine, phenylalanine, norleucine, norvaline or t-butylglycine; 
         R 4  represents a side chain of an amino acid selected from alanine, threonine, serine, valine, t-butylglycine, 2-aminobutyric acid or 2-aminoisobutyric acid; and 
         k and q are individually selected from 1, 2, or 3; or 
         pharmaceutically acceptable salts thereof. 
       
     
     
       2. The compound according to  claim 1 , wherein R 4  represents the side chain of an amino acid selected from alanine, threonine, serine, 2-aminobutyric acid, or 2-aminoisobutyric acid. 
     
     
       3. The compound of claim 2, wherein R 3  represents the side chain of D-leucine; R 4  represents the side chain of 2-aminobutyric acid; R 1  is 2,4-dichlorobenzoyl; k is 2; and q is 1. 
     
     
       4. The compound of claim 1, selected from the group consisting of: 
       
         
           
                 
                 
                 
                 
                 
                 
               
                     
                 
                   Compound  
                   R 1   
                   R 3   
                   R 4   
                   k 
                   q 
                 
                     
                 
                     
                 
                 
                 
                 
                 
                 
                 
               
                   29 
                   4-BPC  
                   D-Leu 
                   Thr 
                   2 
                   2 
                 
                   30 
                   PA 
                   D-Leu  
                   Thr  
                   2 
                   2 
                 
                   56 
                   4-TFMB  
                   D-Leu 
                   Thr 
                   2 
                   1 
                 
                   57 
                   3,4-DCB  
                   D-Leu 
                   Thr  
                   2 
                   1 
                 
                   61 
                   3-CPA 
                   D-Leu 
                   Thr  
                   2 
                   1 
                 
                   62 
                   2,4-DCPA  
                   D-Leu  
                   Thr  
                   2 
                   1 
                 
                   70 
                   2,4-DCPA 
                   D-Leu 
                   Abu  
                   2 
                   1 
                 
                   71  
                   3,4-DCB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   72 
                   2-CB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   73  
                   2-FB 
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   74  
                   4-TFMB  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   75  
                   2-MB  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   76  
                   2-MPA  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   77  
                   4-CPA  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   78  
                   PA  
                   D-Leu  
                   Abu  
                   2  
                   1  
                 
                   79  
                   3-CPA  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   80  
                   4-MPA  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   81  
                   3,4-DCPA  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   82  
                   2,4-DCB  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   83  
                   3,4-DMB  
                   D-Leu  
                   Abu 
                   2 
                   1 
                 
                   84  
                   2-CPA  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   85  
                   2-FPA  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   86  
                   3-FB  
                   D-Leu  
                   Abu  
                   2  
                   1  
                 
                   87  
                   3-MB  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   88  
                   3-CB  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   89  
                   2,4-DMB  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   90  
                   2,3-DCB  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   91  
                   2,3-DMB  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   92  
                   2,4,6-TMB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   93  
                   3,5-DMB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   94 
                   4-CB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   95 
                   2,4,6-TCB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   96  
                   3,5-DCB  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   97  
                   3,5-BTFMB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   98  
                   4-MB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   99  
                   4-IPB  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   100  
                   4-EB  
                   D-Leu  
                   Abu  
                   2  
                   1  
                 
                   101  
                   2-C-4-MB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   102  
                   3-F-4-MB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   103  
                   3,4-DMPA  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   104  
                   4-C-3-MB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   105  
                   3-C-4-MB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   106 
                   3-TFMB  
                   D-Leu  
                   Abu  
                   2  
                   1 
                 
                   107  
                   4-C-3-Fb  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   108  
                   3-F-5-TFMB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   109  
                   2-C-4-TFMB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   110  
                   3-C-4-FB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   111 
                   3-F-4-TFMB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   112 
                   4-C-3-TFMB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   113 
                   4-M-3-TFMB 
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   114 
                   3-C-5-MB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   115 
                   3-C-4-TFMB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   116  
                   3-C-5-FB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   117  
                   3,5-DCB  
                   D-Leu  
                   Ala  
                   2 
                   1 
                 
                   118  
                   3,5-DCB  
                   D-Leu  
                   Thr  
                   2 
                   1 
                 
                   119  
                   3-M-4-TFMB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   120  
                   3-M-5-TFMB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   121  
                   3-TFMB  
                   D-Nle  
                   Abu  
                   2 
                   1 
                 
                   122  
                   3-TFMB  
                   D-Phe 
                   Abu  
                   2 
                   1 
                 
                   123  
                   3-TFMB 
                   D-Nlc 
                   Thr  
                   2 
                   1 
                 
                   124  
                   3-TFMB  
                   D-Phe  
                   Thr  
                   2 
                   1 
                 
                   125  
                   3-TFMB  
                   D-Nlc 
                   Ala  
                   2 
                   1 
                 
                   126  
                   3-TFMB  
                   D-Phe  
                   Ala  
                   2 
                   1 
                 
                   127  
                   4-TFMPA  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   134  
                   4-C-2-FB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   135  
                   2-C-4-FB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   136  
                   4-C-2-TFMB  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   137  
                   2-F-4-TFMB 
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   138  
                   3-BPC  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   141  
                   3-TFMB  
                   D-Leu  
                   Abu  
                   3 
                   1 
                 
                   142  
                   4-BPC 
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   144  
                   4-Cl-BP-4-C 
                   D-Leu  
                   Ala 
                   2 
                   1 
                 
                   145  
                   3-PP  
                   D-Leu  
                   Abu  
                   2 
                   1 
                 
                   146  
                   4-PB  
                   D-Leu  
                   Ala 
                   2 
                   1 
                 
                   147  
                   2,4-DCB  
                   D-Leu  
                   Abu  
                   2 
                   3 
                 
                   148  
                   2,4-DCPS 
                   D-Leu  
                   Abu 
                   2 
                   1, 
                 
                     
                 
             
                
                
                
               
               
                
               
            
             
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
               
            
           
         
       
       or pharmaceutically acceptable salts thereof, wherein 4-BPC=4-biphenylcarboxyl, PA=phenylacetyl, 4-TFMPA=4-trifluoromethylphenylacetyl, 2-MB=2-methylbenzoyl, 3-MB=3-methylbenzoyl, 4-MB=4-methylbenzoyl, 3-F-4-MB=3-fluoro-4-methylbenzoyl, 4-C-3-MB=4-chloro-3-methylbenzoyl, 3-C-4-MB=3-chloro-4-methylbenzoyl, 3-C-5-MB=3-chloro-5-methylbenzoyl, 2-FPA=2-fluorophenylacetyl, 3-TFMB=3-trifuoromethylbenzoyl, 4-TFMB=4-trifluoromethylbenzoyl, 2-C-4-TFMB=2-chloro-4-trifluoromethylbenzoyl, 4-C-3-TFMB=4-chloro-3-trifluoromethylbenzoyl, 3-C-4-TFMB=3-chloro-4-trifluoromethylbenzoyl, 3-F-4-TFMB=3-fluoro-4-trifluoromethylbenzoyl, 3-F-5-TFMB=3-fluoro-5-trifluoromethylbenzoyl, 4-M-3-TFMB=4-methyl-3-trifluoromethylbenzoyl, 3-M-4-TFMB=3-methyl-4-trifluoromethylbenzoyl, 3-M-5-TFMB=3-methyl-5-trifluoromethylbenzoyl, 2-F-4-TFMB=2-fluoro-4-trifluoromethylbenzoyl, 4-C-2-TFMB=4-chloro-2-trifluoromethylbenzoyl, 3,5-BTFMB=3,5-bis(trifluoromethyl)benzoyl, 2,4,6-TMB=2,4,6-trimethylbenzoyl, 2,3-DMB=2,3-dimethylbenzoyl, 2,4-DMB=2,4-dimethylbenzoyl, 3,4-DMB=3,4-dimethylbenzoyl, 3,5-DMB=3,5-dimethylbenzoyl, 2-C-4-MB=2-chloro-4-methylbenzoyl, 4-EB=4-ethylbenzoyl, 4-IPB=4-Isopropylbenzoyl, 2,4-DCPA=2,4-dichlorophenylacetyl, 3,4-DCPA=3,4-dichlorophenylacetyl, 2-CPA=2-chlorophenylacetyl, 3-CPA=3-chlorophenylacetyl, 4-CPA=4-chlorophenylacetyl, 2-CB=2-chlorobenzoyl, 3-CB=3-chlorobenzoyl, 4-CB=4-chlorobenzoyl, 2,3-DCB=2,3-dichlorobenzoyl, 2,4-DCB=2,4-dichlorobenzoyl, 3,4-DCB=3,4-dichlorobenzoyl, 3,5-DCB=3,5-dichlorobenzoyl, 2,4,6-TCB=2,4,6-trichlorobenzoyl, 2-FB=2-fluorobenzoyl, 3-FB=3-fluorobenzoyl, 2-C-4-FB=2-chloro-4-fluorobenzoyl, 3-C-4-FB=3-Chloro-4-fluorobenzoyl, 3-C-5-FB=3-chloro-5-fluorobenzoyl, 4-C-2-FB=4-chloro-2-fluorobenzoyl, 4-C-3-FB=4-chloro-3-fluorobenzoyl, 2-MPA=2-methylphenylacetyl, 4-MPA=4-methylphenylacetyl, 3,4-DMPA=3,4-dimethylphenylacetyl, 3-BPC=3-biphenylcarboxyl, 4-C1-BP-4-C=4-chloro-biphenyl-4-carboxyl, 3-PP=3-phenylproponyl, 4-PB=4-phenylbutanoyl, 2,4-DCPS=2,4-dichlorophenylsulfonyl, Abu=2-aminobutyric acid, Phe=phenylalanine, Thr=threonine, Ala=alanine, Leu=leucine, and Nle=norleucine.

Cited by (0)

No later patents cite this yet.

References (0)

No backward citations on record.